Tag Archives: rarediseses

Dan Marino’s metabolic liver disease highlights growing health concern

Hall of Fame quarterback Dan Marino recently revealed that he was diagnosed with metabolic dysfunction-associated steatohepatitis, or MASH. The Miami Dolphins legend said the discovery came years ago after a routine checkup when he was feeling sluggish. “MASH is a serious form of liver disease characterized by an excessive buildup …

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Scientists may have discovered first gene therapy for incurable brain disease

Scientists may have discovered the first therapy for Huntington’s disease, a brain disorder that until now has had no effective treatments. Researchers at the University of College London (UCL) announced positive results from a global clinical trial for a new gene therapy, AMT-130. Developed by the Dutch biotechnology company uniQure, …

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